MicroRNA-Directed Neuronal Reprogramming as a Therapeutic Strategy for Neurological Diseases.

- 29/06/2017

Therapeutic Strategies Under Development Targeting Inflammatory Mechanisms in Amyotrophic Lateral Sclerosis.

- 28/04/2017

MicroRNA Metabolism and Dysregulation in Amyotrophic Lateral Sclerosis.

- 18/04/2017

Genome-wide RNA-seq of iPSC-derived motor neurons indicates selective cytoskeletal perturbation in Brown-Vialetto disease that is partially rescued by riboflavin.

- 06/04/2017

iPSC-derived LewisX+CXCR4+β1-integrin+ neural stem cells improve the amyotrophic lateral sclerosis phenotype by preserving motor neurons and muscle innervation in human and rodent models.

- 01/08/2016

Development of Therapeutics for C9ORF72 ALS/FTD-Related Disorders.

- 28/06/2016

Differential neuronal vulnerability identifies IGF-2 as a protective factor in ALS.

- 16/05/2016

Experimental Advances Towards Neural Regeneration from Induced Stem Cells to Direct In Vivo Reprogramming.

- 01/05/2016

Autophagy in motor neuron disease: Key pathogenetic mechanisms and therapeutic targets.

- 01/04/2016

Morpholino-mediated SOD1 reduction ameliorates an amyotrophic lateral sclerosis disease phenotype.

- 16/02/2016

Clinical and molecular features and therapeutic perspectives of spinal muscular atrophy with respiratory distress type 1.

- 19/09/2015

MFN2-related neuropathies: Clinical features, molecular pathogenesis and therapeutic perspectives.

- 15/09/2015

SOD1 misplacing and mitochondrial dysfunction in amyotrophic lateral sclerosis pathogenesis.

- 25/08/2015

Spinal muscular atrophy phenotype is ameliorated in human motor neurons by SMN increase via different novel RNA therapeutic approaches.

- 30/06/2015

Human pluripotent stem cells as tools for neurodegenerative and neurodevelopmental disease modeling and drug discovery.

- 15/06/2015

Spinal muscular atrophy–recent therapeutic advances for an old challenge.

- 11/06/2015

Motor neurons with differential vulnerability to degeneration show distinct protein signatures in health and ALS.

- 16/04/2015

Gene therapy rescues disease phenotype in a spinal muscular atrophy with respiratory distress type 1 (SMARD1) mouse model.

- 13/03/2015

Therapeutic development in amyotrophic lateral sclerosis.

- 01/03/2015

Pluripotent stem cell-based models of spinal muscular atrophy

- 10/01/2015

Therapeutic applications of the cell-penetrating HIV-1 Tat peptide

- 01/01/2015

Antisense oligonucleotide therapy for the treatment of C9ORF72 ALS/FTD diseases

- 01/12/2014

The wide spectrum of clinical phenotypes of spinal muscular atrophy with respiratory distress type 1: a systematic review

- 15/11/2014

iPSC-Based Models to Unravel Key Pathogenetic Processes Underlying Motor Neuron Disease Development

- 17/10/2014

Stem cell transplantation for amyotrophic lateral sclerosis: therapeutic potential and perspectives on clinical translation.

- 01/09/2014

iPSC-Derived neural stem cells act via kinase inhibition to exert neuroprotective effects in spinal muscular atrophy with respiratory distress type 1.

- 12/08/2014

Motor neuron derivation from human embryonic and induced pluripotent stem cells: experimental approaches and clinical perspectives.

- 14/07/2014

In vitro neurogenesis: development and functional implications of iPSC technology.

- 01/05/2014

Induced neural stem cells: methods of reprogramming and potential therapeutic applications.

- 15/03/2014

Cellular therapy to target neuroinflammation in amyotrophic lateral sclerosis.

- 07/03/2014

Effect of combined systemic and local morpholino treatment on the spinal muscular atrophy Δ7 mouse model phenotype.

- 01/03/2014

Molecular therapeutic strategies for spinal muscular atrophies: current and future clinical trials.

- 01/01/2014

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